Title | Targeting RNA foci in iPSC-derived motor neurons from ALS patients with a C9ORF72 repeat expansion. |
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Authors | Sareen D, O'Rourke JG, Meera P, Muhammad AK, Grant S, Simpkinson M, Bell S, Carmona S, Ornelas L, Sahabian A, Gendron T, Petrucelli L, Baughn M, Ravits J, Harms MB, Rigo F, Bennett CF, Otis TS, Svendsen CN, Baloh RH |
Journal | Sci Transl Med |
Year | 2013 |
Volume | 5 |
Issue | 208 |
Pages | 208ra149 |
URL | http://www.ncbi.nlm.nih.gov/pubmed/24154603 |
PubMed ID | 24154603 |
DOI | 10.1126/scitranslmed.3007529 |